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Protected: Advancing breakthrough science into life-changing medicines for rare disease

Protected: More Than You Can Imagine: The Unseen Work That Gets Rare Disease Medicines to Patients

Protected: Rare but costly: the importance of defining the true cost of rare diseases in the UK

Protected: Meet Mollie

Rare Diseases Q1 2026

Protected: Why Clinical Trials Matter — Especially for Rare Diseases

Rare Diseases Q1 2026

Protected: How we’re using artificial intelligence to advance rare disease research

Protected: How collaboration and innovation are advancing rare disease care

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Protected: Why mRNA medicines could be a rare disease breakthrough

Rare Diseases Q1 2026

Protected: Connecting Europe for rare diseases

Rare Diseases Q1 2026

Protected: Healthcare equity for rare conditions

Protected: Reshaping access to rare disease medicines to ensure no one is left behind

Rare Diseases Q1 2026

Protected: The future is now: how young people are shaping the future of rare disease advocacy

Rare Diseases Q1 2026

Protected: Changing the future of healthcare through genomics

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Rare Diseases Q1 2026

Protected: Youth Driving Global Rare Disease Change

Rare Diseases Q1 2026

Protected: Closing the global diagnosis gap

Rare Diseases Q1 2026

Protected: Call for rare disease global action

Rare Diseases Q1 2026

Protected: Turning rare disease data into actionable knowledge

Rare Diseases Q1 2026

Protected: Rare disease and the undeniable force of patient advocacy

Rare Diseases Q1 2026

Protected: Supporting those who carry the weight of rare disease

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Two nurses using a computer in a x-ray room

The role of rare disease education in the diagnostic odyssey

Redefining the rare disease launch to reach every patient

Rare Diseases 2025

The vision for a competitive Europe that rare diseases offer

Family in the park on bicycles. two sibling brothers kids boys compete in riding. view from back

Connecting, cycling and changing children’s lives

Vibrant blood test tubes are arranged neatly in a sleek holder, showcasing their unique colors and caps, symbolizing the critical role of laboratory testing in health assessments and diagnostics

Rare Diseases 2025

Diagnosing the world’s forgotten children through genomic testing